A CRISPR-Cas9-based therapy targeting the gene encoding transthyretin greatly reduced transthyretin levels in patients with ...

Eli Lilly LLY and AbbVie ABBV are large, well-established U.S. pharmaceutical companies, boasting several blockbuster drugs, ...

Odyssey Therapeutics, Inc., a clinical-stage biopharmaceutical company seeking to transform the standard of care for patients ...

Musunuru provided ESGCT delegates with promising news of a roadmap following the diagnosis and treatment of Baby KJ.

As industry leaders gather at the annual event in Phoenix, the cell and gene therapy space remains in a state of flux, with M ...